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The FDA approved a new gene therapy for Sanfilippo syndrome type A, an ultra-rare disease sometimes known as childhood Alzheimer’s.
Lees bij STAT News · 17 september 2026 om 19:55
Researchers have identified a very rare genetic variant that is associated with higher odds of lung cancer in "never smokers."
Lees bij STAT News · 17 september 2026 om 18:00
A psychedelic-like drug for a Parkinson's symptom, mice with half-human brains, and more biotech news in the Readout newsletter.
Lees bij STAT News · 17 september 2026 om 14:30
In this edition of STAT Health Tech: Zocdoc enables appointment scheduling from chatbots and health plan websites, and more.
Lees bij STAT News · 17 september 2026 om 13:09